uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 20, 2020
RegMed Investors’ (RMi) closing bell: sector slips again post earnings' blues, we need news and catalysts
August 20, 2020
RegMed Investors’ (RMi) pre-open: volatility is chewing on the sector resulting in oversold conditions in some
August 18, 2020
RegMed Investors’ (RMi) closing bell: sector sells-off
August 18, 2020
RegMed Investors’ (RMi) pre-open: an opening gain projected
August 14, 2020
RegMed Investors’ (RMi) closing bell: yet another sector rotation to the downside
August 12, 2020
RegMed Investors’ (RMi) closing bell: another slump
August 12, 2020
RegMed Investors’ (RMi) pre-open: strap in, the roller-coaster sector causes a gut-churn
August 7, 2020
RegMed Investors’ (RMi) closing bell: anxiety was overcome as the oversold got supported
August 7, 2020
RegMed Investors’ (RMi) pre-open: jobs report and executive orders creates anxiety in markets
35 companies, 1 interpreter!
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