uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 24, 2019
RegMed Investors’ (RMi) closing bell: pleasantly surprised as the sector flipped to the upside
July 23, 2019
RegMed Investors’ (RMi) closing bell: the sector is locked away in the bottom, again
July 23, 2019
RegMed Investors’ (RMi) pre-open: another mild tailwind
July 22, 2019
RegMed Investors’ (RMi) closing bell: the upside swelled from Friday’s decline
July 19, 2019
RegMed Investors’ (RMi) closing bell: expiration of options amplified the sector’s selloff
July 18, 2019
RegMed Investors’ (RMi) closing bell: wow, another sustaining session
July 17, 2019
RegMed Investors’ (RMi) closing bell: lucky, lucky the sector rose
July 16, 2019
RegMed Investors’ (RMi) closing bell: Expectations are low in share pricing
July 15, 2019
RegMed Investors’ (RMi) closing bell: a new week’s session flutters with low volume
35 companies, 1 interpreter!
Insight, foresight and recommendation
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