uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
December 18, 2017
RegMed Investors’ (RMi) pre-open indication: hopefully the witch busted its broom
December 15, 2017
RegMed Investors’ (RMi) closing bell; sector opened down, stayed depressed at the mid-day and closed neutral
December 14, 2017
RegMed Investors’ (RMi) closing bell; sector drifts downward on low volume
December 13, 2017
RegMed Investors’ (RMi) closing bell; the sector closed up and positive with a 30/8 advance/decline line
December 12, 2017
RegMed Investors’ (RMi) closing bell; sentiment is more than a threat
December 12, 2017
RegMed Investors’ (RMi) pre-open indication: struggling for pricing position
December 11, 2017
RegMed Investors’ (RMi) closing bell; ASH giveth and taketh
December 8, 2017
RegMed Investors’ (RMi) closing bell; the newest version of an old normal
December 7, 2017
RegMed Investors’ (RMi) closing bell; finally an upside
December 6, 2017
RegMed Investors’ (RMi) closing bell; another day of woe to a cell therapy portfolio
35 companies, 1 interpreter!
Insight, foresight and recommendation
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