uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 14, 2016
RegMed’s close: The sector corrects ...
January 13, 2016
RegMed’s close: JPM didn’t pass out enough lipstick
January 12, 2016
The market has NOT been kind ...
January 8, 2016
RegMed’s close: There's a lot of activity in the sector - good, bad and ugly
January 7, 2016
RegMed’s close: volatility is frightening
January 7, 2016
UniQure’s (QURE) gene therapy boosts clotting in two Hemophiliacs
January 5, 2016
RegMed’s close: up, down and down again, a rally and momentum was short-lived
December 31, 2015
RegMed’s close: the last day of trading expires
December 30, 2015
RegMed’s close: with little volume, it's easy to move the sector either way
December 28, 2015
RegMed’s close: lower as traders cull any upside
35 companies, 1 interpreter!
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