uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
February 25, 2025
RegMed Investors (RMi) Closing Bell: sector suffers further share pricing weakening
February 24, 2025
RegMed Investors (RMi) Closing Bell: faked out by Monday’s sector, close even I
February 21, 2025
RegMed Investors (RMi) Closing Bell: Stare into the abyss to see the cell and gene therapy share pricing remains after initial positive open
February 20, 2025
RegMed Investors (RMi) Closing Bell: Sector bends to econs yet again
February 19, 2025
RegMed Investors (RMi) Closing Bell: a sign, advanced/decline line is dropping!
February 18, 2025
RegMed Investors (RMi) Closing Bell: market and sector’s hovering
February 14, 2025
RegMed Investors (RMi) Closing Bell: got some, the end of the session and week
February 13, 2025
RegMed Investors (RMi) Closing Bell: chew, eat and digest
February 12, 2025
RegMed Investors (RMi) Closing Bell: walking the line
February 11, 2025
RegMed Investors (RMi) Closing Bell: the sector gets further mutilated
35 companies, 1 interpreter!
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