uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 15, 2021
RegMed Investors’ (RMi) closing bell: sector declines - it’s not transitory, infamous current terms
November 15, 2021
RegMed Investors’ (RMi) pre-open: After last week's market losses, how should investors respond?
November 12, 2021
RegMed Investors’ (RMi) closing bell: gravity is more than a force, it’s a sector disorder
November 12, 2021
RegMed Investors’ (RMi) pre-open: another quick exit Friday after six (6) negative closes?
November 11, 2021
RegMed Investors’ (RMi) closing bell: from an extreme downside to a barely downslide
November 11, 2021
RegMed Investors’ (RMi) pre-open: a weak aftermarket underwhelms expectation
November 10, 2021
RegMed Investors’ (RMi) closing bell: yet another pull-back that cut to the bone as the sector bleeds-out
November 10, 2021
RegMed Investors’ (RMi) pre-open: sector weakness should/could unfold some of the oversold
November 9, 2021
RegMed Investors’ (RMi) closing bell: sector takes yet another dive
November 9, 2021
RegMed Investors’ (RMi) pre-open: a sector retreat is not a defeat, it will just move directionally
35 companies, 1 interpreter!
Insight, foresight and recommendation
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