uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 8, 2021
RegMed Investors’ (RMi) closing bell: the sector faded even as small-cap stocks led on the upside and held near their highs
November 8, 2021
RegMed Investors’ (RMi) pre-open: "Skip to My (The) Lou" after a record close, a sector decline, more LPS (loss-per-share) earnings this week
November 6, 2021
RegMed Investors’ (RMi) closing bell: bag and tag ‘em, as LPS (loss-per-share) earnings define the week’s share pricing endings
November 5, 2021
RegMed Investors’ (RMi) pre-open: not so fast to the sector exit on Friday but, I'm still walking instead of running
November 4, 2021
RegMed Investors’ (RMi) closing bell: not quite wrong and almost totally correct
November 4, 2021
RegMed Investors’ (RMi) pre-open: there are sessions I am out-on-the-limb having brought a saw with me
November 3, 2021
RegMed Investors’ (RMi) closing bell: markets and sector, the big casino
November 3, 2021
RegMed Investors’ (RMi) pre-open: is today, a post earnings response and some more
November 2, 2021
RegMed Investors’ (RMi) closing bell: you say what, I say why
November 2, 2021
RegMed Investors’ (RMi) pre-open: time to show their cards
35 companies, 1 interpreter!
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