uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
April 13, 2020
RegMed Investors’ (RMi) closing bell: never bend down for a falling knife, it could bounce off the tile and draw blood
April 13, 2020
RegMed Investors’ (RMi) pre-open: it’s coming, expect a retest of the market’s March low
April 11, 2020
Regenerative Medicine Earnings Scorecard - Q4 & FY19
April 9, 2020
RegMed Investors’ (RMi) closing bell: thanks for the upside, sell into the upside strength although volume is low
April 8, 2020
RegMed Investors’ (RMi) closing bell: markets are stuck in the middle of anticipation
April 7, 2020
RegMed Investors’ (RMi) closing bell: markets lose their steam minutes from the close as the sector gets ahead of reality
April 6, 2020
RegMed Investors’ (RMi) closing bell: a stabilizing event is needed in infection and death rates
April 3, 2020
RegMed Investors’ (RMi) closing bell: any gains have vanished from continued weakness
April 2, 2020
RegMed Investors’ (RMi) closing bell: What is not priced in?
April 1, 2020
RegMed Investors’ (RMi) closing bell: the cell/gene sector baby programs are being disregarded and tossed with the bathwater
35 companies, 1 interpreter!
Insight, foresight and recommendation
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