uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
March 25, 2020
RegMed Investors’ (RMi) closing bell: stimulus inspires markets another 5% gain after Tuesday’s 11% incline
March 24, 2020
RegMed Investors’ (RMi) closing bell: cell and gene therapy recover as volume moves the ladder of inclines
March 23, 2020
RegMed Investors’ (RMi) closing bell: a distressed market influences the cell and gene therapy sector
March 20, 2020
RegMed Investors’ (RMi) closing bell: whiplash, fear, panic and quadruple witching fuel volatility
March 19, 2020
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector rises like the mythological phoenix
March 19, 2020
RegMed Investors’ (RMi) pre-open: bada bing bada boom and calling it as it should be the Wuhan virus from where it emanated
March 18, 2020
RegMed Investors’ (RMi): another liquidity scramble as volatility speeds through open lanes of resistance
March 13, 2020
RegMed Investors’ (RMi): the sector carousel kept turning after dips stopped and upside motion re-started
March 6, 2020
RegMed Investors’ (RMi): a big blip with a moderate comeback or a black swan
35 companies, 1 interpreter!
Insight, foresight and recommendation
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