uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
March 3, 2020
RegMed Investors’ (RMi) pre-open: uncertainty unsettles markets, I’ve been scratching the selling and profiteering itch
March 2, 2020
RegMed Investors’ (RMi) closing bell: markets are jumping and bringing the sector along for the ride
March 2, 2020
RegMed Investors’ (RMi) pre-open: another volatile start to the week
February 28, 2020
RegMed Investors’ (RMi) closing bell: my coverage sector closed positive showing share pricing life
February 27, 2020
RegMed Investors’ (RMi) closing bell: wild sector overreacts with panic in sentiment and market breadth by coronavirus fright and dread
February 26, 2020
RegMed Investors’ (RMi) closing bell: sector struggles as rebound slips
February 25, 2020
RegMed Investors’ (RMi) closing bell: parabolic moves to the downside
February 19, 2020
RegMed Investors’ (RMi) closing bell: are investors listening, earning’s season leaves whispers all through this and next month
February 18, 2020
RegMed Investors’ (RMi) closing bell: today is a call for investors to categorize the market and sector’s undercurrents
35 companies, 1 interpreter!
Insight, foresight and recommendation
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