uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 21, 2019
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August 20, 2019
RegMed Investors’ (RMi) closing bell: the sector dike sprung a leak and equities poured-out
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RegMed Investors’ (RMi) pre-open: skim if you can trim, buy if it will fly and sell if compelled!
August 19, 2019
RegMed Investors’ (RMi) closing bell: the sector rallied
August 13, 2019
RegMed Investors’ (RMi) closing bell: the sector flipped up but, didn’t soar
August 10, 2019
RegMed Investors’ (RMi) closing bell: after the sessions and week’s numbers, there’s still a directional signal for the new periods coming
August 8, 2019
RegMed Investors’ (RMi) closing bell: the daily dose of share pricing
August 6, 2019
RegMed Investors’ (RMi) closing bell: the sector recuperated after a bad session
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RegMed Investors’ (RMi) closing bell: another wipe-out of sector value
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Regenerative Medicine Earnings Scorecard - Q2/19 - to date
35 companies, 1 interpreter!
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