uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 29, 2019
RegMed Investors’ (RMi) pre-open: trade the recent highs
July 26, 2019
RegMed Investors’ (RMi) closing bell: the sector jumps as NASDAQ records another record close
July 26, 2019
RegMed Investors’ (RMi) pre-open: closer and closer
July 25, 2019
RegMed Investors’ (RMi) closing bell: slow is smooth, smooth is fast
July 25, 2019
RegMed Investors’ (RMi) pre-open: sit, seek sanctuary or lock-in a de-risked position pre-earnings release?
July 24, 2019
RegMed Investors’ (RMi) closing bell: pleasantly surprised as the sector flipped to the upside
July 23, 2019
RegMed Investors’ (RMi) closing bell: the sector is locked away in the bottom, again
July 23, 2019
RegMed Investors’ (RMi) pre-open: another mild tailwind
July 22, 2019
RegMed Investors’ (RMi) closing bell: the upside swelled from Friday’s decline
35 companies, 1 interpreter!
Insight, foresight and recommendation
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