uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
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May 14, 2019
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RegMed Investors’ (RMi) closing bell: there was share pricing blood on the floor and spatter on the walls
May 13, 2019
RegMed Investors’ (RMi) pre-open: time for some sector movement even with the current levels of market uncertainty
May 10, 2019
RegMed Investors’ (RMi) closing bell: trade is also the sector’s issue while the IBB (-0.32%) slips
May 9, 2019
RegMed Investors’ (RMi) closing bell: another session of drip, drip and another dip
May 3, 2019
RegMed Investors’ (RMi) pre-open: now that it’s May, employment data sounds off
May 2, 2019
RegMed Investors’ (RMi) closing bell: after a flip, a flop and another drop
May 2, 2019
RegMed Investors’ (RMi) pre-open: insight is about understanding perception
35 companies, 1 interpreter!
Insight, foresight and recommendation
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