uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
May 1, 2019
RegMed Investors’ (RMi) closing bell: another downturn as the NASDAQ stumbled into the close
May 1, 2019
RegMed Investors’ (RMi) pre-open: first trading day of the month of May
April 30, 2019
RegMed Investors’ (RMi) pre-open: Pharma’s report, Merck (MRK), Ely Lilly (LLY) and Pfizer (PFE)
April 29, 2019
RegMed Investors’ (RMi) closing bell: fundamentals are improving as sentiment edges the sector higher
April 29, 2019
RegMed Investors’ (RMi) pre-open: inversion or transposition
April 26, 2019
RegMed Investors’ (RMi) closing bell: the sector rose on an oversold prompt and closed to the upside
April 25, 2019
RegMed Investors’ (RMi) closing bell: sector equities got-up off their knees!
April 24, 2019
RegMed Investors’ (RMi) closing bell: sector moves, a slip and a fall
April 23, 2019
RegMed Investors’ (RMi) closing bell: sector rallies with volatility in our favor
April 22, 2019
RegMed Investors’ (RMi) closing bell: session’s description – weakness, Advance/Decline (A/D) line deterioration with low volume
35 companies, 1 interpreter!
Insight, foresight and recommendation
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