uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 29, 2019
RegMed Investors’ (RMi) pre-open: sector risks vary resulting from low volume and steep declines
January 28, 2019
RegMed Investors’ (RMi) closing bell: retracement is more than a temporary reversal
January 24, 2019
RegMed Investors’ (RMi) closing bell: sector jumps making up for ground lost as the risk appetite dwindles or does it?
January 24, 2019
RegMed Investors’ (RMi) pre-open: I’m sticking to an oversold sector thesis
January 23, 2019
RegMed Investors’ (RMi) closing bell: oversold with a lack of volume, absent momentum and no retest of bottoms
January 23, 2019
RegMed Investors’ (RMi) pre-open: the phoenix rises as “some” of the CRISPRs upsurge
January 22, 2019
RegMed Investors’ (RMi) closing bell: the CRISPR sell-off
January 22, 2019
RegMed Investors’ (RMi) pre-open: performance anxiety
January 18, 2019
RegMed Investors’ (RMi) pre-open: selective evidence
January 17, 2019
RegMed Investors’ (RMi) closing bell: risky business
35 companies, 1 interpreter!
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