uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 16, 2019
RegMed Investors’ (RMi) closing bell: where is the buzz?
January 14, 2019
RegMed Investors’ (RMi) closing bell: today, it’s about playing the trading ranges after back-to-back negative closes!
January 2, 2019
RegMed Investors’ (RMi) closing bell: Trading jumped-on the oversold condition
December 28, 2018
RegMed Investors’ (RMi) closing bell: sector stocks are volume centric and sensitive
December 24, 2018
RegMed Investors’ (RMi) closing bell: a shorten session that went deep to the downside yet, the sector saw some upside
December 19, 2018
RegMed Investors’ (RMi) closing bell: Nobody likes this market!
December 17, 2018
RegMed Investors’ (RMi) closing bell: escaping the downside in this market, is pure luck even for those equities with news!
December 17, 2018
RegMed Investors’ (RMi) pre-open: Who do you call for “share side” assistance? It’s not AAA, try RMi …
December 14, 2018
RegMed Investors’ (RMi) closing bell: sentiment elevators down while pricing action takes the escalator down
35 companies, 1 interpreter!
Insight, foresight and recommendation
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