uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 23, 2018
RegMed Investors’ (RMi) closing bell: memo to Investors: what goes UP will come DOWN
August 23, 2018
RegMed Investors’ (RMi) closing bell: memo to Investors: what goes UP will come DOWN
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RegMed Investors’ (RMi) closing bell: hop, skip and a few slips
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RegMed Investors’ (RMi) pre-open: hoping and praying for a rebound of the oversold
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RegMed Investors’ (RMi) closing bell: the sector stumbled
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RegMed Investors’ (RMi) closing bell; the impact of August, earnings, low volume and high volatility
August 8, 2018
RegMed Investors’ (RMi) closing bell; sentiment played-in and faded out
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RegMed Investors’ (RMi) pre-open: what and how do we value?
35 companies, 1 interpreter!
Insight, foresight and recommendation
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