uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 6, 2018
RegMed Investors’ (RMi) closing bell; catch and release is also about share price weighing
August 2, 2018
RegMed Investors’ (RMi) closing bell; after a session of bouncing around, Q2 results recover share pricing losses
August 1, 2018
RegMed Investors’ (RMi) closing bell; what goes up precipitately, verves down as easy
July 30, 2018
RegMed Investors’ (RMi) closing bell; is the sector suffering from investor impotence
July 19, 2018
RegMed Investors’ (RMi) closing bell: the carousel of investing, sentiment is like music, trading turns it on and off
July 19, 2018
RegMed Investors’ (RMi) closing bell: the carousel of investing, sentiment is like music turns it on and off
July 19, 2018
RegMed Investors’ (RMi) closing bell: the carousel of investing, sentiment is like music turns it on and off
July 18, 2018
RegMed Investors’ (RMi) closing bell: the thumb-screws are still on gene editing equities
July 17, 2018
RegMed Investors’ (RMi) closing bell: gene editing stocks bounce back
35 companies, 1 interpreter!
Insight, foresight and recommendation
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