uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 2, 2018
RegMed Investors’ (RMi) closing bell: Q3 starts with a boom and a broom
June 29, 2018
RegMed Investors’ (RMi) closing bell: final trading day of the month and end to the quarter
June 29, 2018
RegMed Investors’ (RMi) pre-open; let June and the quarter go quietly
June 28, 2018
RegMed Investors’ (RMi) closing bell: another wild ride as rotation continued to envelope the sector
June 28, 2018
RegMed Investors’ (RMi) pre-open; waiting for (a signal) Godot
June 22, 2018
RegMed Investors’ (RMi) closing bell: action and reaction; the good, the bad and the ugly
June 21, 2018
RegMed Investors’ (RMi) closing bell: home in the sector’s range follow-on lyrics …
June 21, 2018
RegMed Investors’ (RMi) pre-open; “home in the sector's range”
June 20, 2018
RegMed Investors’ (RMi) closing bell: what’s considered expensive in the sector?
June 20, 2018
RegMed Investors’ (RMi) pre-open; some big jumps and dives in pricing
35 companies, 1 interpreter!
Insight, foresight and recommendation
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