uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 19, 2018
RegMed Investors’ (RMi) closing bell: pick a move
June 19, 2018
RegMed Investors’ (RMi) pre-open; pre-open indications slump and dump
June 18, 2018
RegMed Investors’ (RMi) closing bell: the overbought are getting riper
June 15, 2018
RegMed Investors’ (RMi) closing bell: whole lot of covering going-on
June 14, 2018
RegMed Investors’ (RMi) closing bell: beware of the NASDAQ bearing gains
June 13, 2018
RegMed Investors’ (RMi) closing bell: the sector closes barely positive
June 12, 2018
RegMed Investors’ (RMi) closing bell: no surprises
June 11, 2018
RegMed Investors’ (RMi) pre-open; tick, tick; when is the tock
June 9, 2018
RegMed Investors’ (RMi) closing bell: after the storm, there was a neutral calm upon the sector
35 companies, 1 interpreter!
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