uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
April 17, 2018
RegMed Investors’ (RMi) closing bell; trading ranges flirt with the upside as the sector’s oversold surge
April 16, 2018
RegMed Investors’ (RMi) closing bell; losses chain the sector together
April 16, 2018
RegMed Investors’ (RMi) pre-open: a bounce is upon us?
April 13, 2018
RegMed Investors’ (RMi) closing bell; the sector slipped
April 13, 2018
RegMed Investors’ (RMi) pre-open: minor gains in futures with IBB slippage
April 12, 2018
RegMed Investors’ (RMi) closing bell; the force was with the sector
April 12, 2018
RegMed Investors’ (RMi) pre-open: reap the harvest of the upside, sell or buy into capricious strength?
April 11, 2018
RegMed Investors’ (RMi) closing bell; sector pricing withers
April 10, 2018
RegMed Investors’ (RMi) closing bell; chugging along
April 10, 2018
RegMed Investors’ (RMi) pre-open: buckle up
35 companies, 1 interpreter!
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