uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
March 23, 2018
RegMed Investors’ (RMi) closing bell; swing low, coming for to carry me down
March 23, 2018
RegMed Investors’ (RMi) pre-open: trade jitters spook markets
March 22, 2018
RegMed Investors’ (RMi) closing bell; the sell-off returns
March 22, 2018
RegMed Investors’ (RMi) pre-open: historical data can’t always determine current events
March 21, 2018
RegMed Investors’ (RMi) closing bell; sector regains its footing
March 21, 2018
RegMed Investors’ (RMi) pre-open: the gap in trading ranges
March 20, 2018
RegMed Investors’ (RMi) closing bell; the bounce back is small but, happening
March 19, 2018
RegMed Investors’ (RMi) closing bell; markets take a hit as the NASDAQ drags down the sector
March 15, 2018
RegMed Investors’ (RMi) closing bell; swimming against the tide
March 14, 2018
RegMed Investors’ (RMi) closing bell; what started up, ended with another slip and fall
35 companies, 1 interpreter!
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