uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
March 4, 2018
RegMed Investors’ (RMi) wrapping-up January and February while determining March’s strength …
March 2, 2018
RegMed Investors’ (RMi) closing bell; the oversold jumped as the panic subsided
March 1, 2018
RegMed Investors’ (RMi) closing bell; the sector got spooked by the market sell-off
February 28, 2018
RegMed Investors’ (RMi) closing bell; sector traded up until the last hour
February 27, 2018
RegMed Investors’ (RMi) closing bell; sector trips to the downside
February 26, 2018
RegMed Investors’ (RMi) closing bell; the velocity of pricing movement
February 23, 2018
RegMed Investors’ (RMi) closing bell; sector reverses losses late afternoon
February 23, 2018
RegMed Investors’ (RMi) pre-open: nervous after two (2) dramatic upside sessions
February 22, 2018
RegMed Investors’ (RMi) closing bell; the trading “tourists” stuck to the schedule
February 21, 2018
RegMed Investors’ (RMi) closing bell; a comeback
35 companies, 1 interpreter!
Insight, foresight and recommendation
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