uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
February 20, 2018
RegMed Investors’ (RMi) closing bell; sector weakens
February 16, 2018
RegMed Investors’ (RMi) closing bell; a flip-flop is edge-sensitive
February 15, 2018
RegMed Investors’ (RMi) closing bell; finding the path to the least resistance
February 14, 2018
RegMed Investors’ (RMi) closing bell; sector reverses to trade higher erasing losses
February 7, 2018
RegMed Investors’ (RMi) closing bell; recovery with stronger gains while volatility is still high
February 6, 2018
RegMed Investors’ (RMi) closing bell; sector reverses and flip-flops by the hour
February 6, 2018
RegMed Investors’ (RMi) pre-open: the tumble down game
February 5, 2018
RegMed Investors’ (RMi) closing bell; be very careful in buying any dips
February 2, 2018
RegMed Investors’ (RMi) closing bell; volatility is raining on share pricing without an umbrella
February 2, 2018
RegMed Investors’ (RMi) pre-open: the known unknowns as the market is headed for a big sell-off
35 companies, 1 interpreter!
Insight, foresight and recommendation
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