uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 23, 2018
RegMed Investors’ (RMi) pre-open: the “JUNO” effect
January 22, 2018
RegMed Investors’ (RMi) closing bell; Celgene’s (CELG) acquisition renews interest in cell therapy
January 22, 2018
RegMed Investors’ (RMi) pre-open: riding the upside as Celgene (CELG) prices acquisition of Juno Therapeutics (JUNO) at $87 per share or $9 B
January 19, 2018
RegMed Investors’ (RMi) closing bell; the sector has a crisis in confidence
January 17, 2018
RegMed Investors’ (RMi) closing bell; selling the rips until the mid-day recognized the oversold and closed barely positive
January 12, 2018
RegMed Investors’ (RMi) closing bell; rebound followed by a relapse
January 11, 2018
RegMed Investors’ (RMi) closing bell; expectation, a strong belief that something will happen or not, it’s still an assumption
January 10, 2018
RegMed Investors’ (RMi) closing bell; more of same, an effervesce without any fizz
January 9, 2018
RegMed Investors’ (RMi) closing bell; sentiment and volatility are still the judge and jury while the healthcare conference rolls on
January 8, 2018
RegMed Investors’ (RMi) closing bell; what happened to the healthcare conference’s jump start of the sector?
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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