uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 20, 2025
RegMed Investors (RMi) Closing Bell: Luckily, the canopy opened
June 18, 2025
RegMed Investors (RMi) Closing Bell: a sector of flash bang pricing movements
June 17, 2025
RegMed Investors (RMi) Closing Bell: I love the smell of gene therapy sentiment in the morning!!
June 16, 2025
RegMed Investors (RMi) Closing Bell: My view/words ring true
June 13, 2025
RegMed Investors (RMi) Closing Bell: sector bottoms evident as collateral damage
June 12, 2025
RegMed Investors (RMi) Closing Bell: Present value in the cell and gene therapy share pricing reflects the sector’s acrobatics
June 11, 2025
RegMed Investors (RMi) Closing Bell: inflationary econ was soft, thumping markets and tripping sector
June 10, 2025
RegMed Investors (RMi) Closing Bell: got it up
June 9, 2025
RegMed Investors (RMi) Closing Bell: sector momentum waned
June 6, 2025
RegMed Investors (RMi) Closing Bell: surprise, a positive open and close
35 companies, 1 interpreter!
Insight, foresight and recommendation
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