uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 3, 2017
RegMed Investors’ (RMi) pre-open indications; tread lightly
October 2, 2017
RegMed Investors’ (RMi) closing bell; the month starts on a good note
September 29, 2017
RegMed Investors’ (RMi) closing bell; the month and quarter close positive
September 28, 2017
RegMed Investors’ (RMi) closing bell; this dip needed to be bought
September 27, 2017
RegMed Investors’ (RMi) closing bell; Yippee-Ki-Yay
September 26, 2017
RegMed Investors’ (RMi) closing bell; just when some thought it was safe to enter the sector …
September 25, 2017
RegMed Investors’ (RMi) closing bell; be careful for the upside you’ve wished for
September 22, 2017
RegMed Investors’ (RMi) closing bell; sector gets downsized again
September 22, 2017
RegMed Investors’ (RMi) pre-open indications; pricing hunkers down
September 21, 2017
RegMed Investors’ (RMi) closing bell; bowling for strikes, it’s all in the approach
35 companies, 1 interpreter!
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