uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 20, 2017
RegMed Investors’ (RMi) closing bell; shareholder populism is on the rise and companies better adapt
September 18, 2017
RegMed Investors’ (RMi) closing bell; the sector traded higher
September 12, 2017
RegMed Investors’ (RMi) closing bell; the sector trips
September 11, 2017
RegMed Investors’ (RMi) closing bell; volume is spasmodic while momentum is fickle and evasive
September 6, 2017
RegMed Investors’ (RMi) closing bell; this week, Verastem’s (VSTM) results driven upside causes a sector weakness thread
September 5, 2017
RegMed Investors’ (RMi) closing bell; another bubble has burst
September 1, 2017
RegMed Investors’ (RMi) closing bell; cell and gene therapy equities are slow movers or down
August 31, 2017
RegMed Investors’ (RMi) closing bell; the sector was rising
August 30, 2017
RegMed Investors’ (RMi) closing bell; Novartis (NVS) moves today’s sector
August 29, 2017
RegMed Investors’ (RMi) closing bell; buying opportunities?
35 companies, 1 interpreter!
Insight, foresight and recommendation
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