uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 24, 2017
RegMed Investors’ (RMi) closing bell; here we go again…
August 23, 2017
RegMed Investors’ (RMi) closing bell; sector was up
August 22, 2017
RegMed Investors’ (RMi) closing bell; today’s bounce back sector is …
August 21, 2017
RegMed Investors’ (RMi) closing bell; sector takes another dive
August 17, 2017
RegMed Investors’ (RMi) closing bell; sector stumbles
August 16, 2017
RegMed Investors’ (RMi) closing bell; sector trips to a neutral location
August 9, 2017
RegMed Investors’ (RMi) closing bell, who was betting today?
August 9, 2017
Regenerative Medicine Earnings Scorecard - Q2/2017 - to date
August 8, 2017
RegMed Investors’ (RMi) closing bell, is cell therapy losing its individual investor base
August 8, 2017
RegMed Investors’ (RMi) pre-open indications, turbulence coming
35 companies, 1 interpreter!
Insight, foresight and recommendation
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