uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 14, 2017
RegMed Investors’ (RMi) closing bell, where good news goes to die
June 13, 2017
RegMed Investors’ (RMi) closing bell, another I told you so …
June 12, 2017
RegMed Investors’ (RMi) closing bell, headwinds abound
June 10, 2017
RegMed Investors’ (RMi) closing bell, it was time to make a deposit …
June 8, 2017
RegMed Investors’ (RMi) closing bell, political words were a basis for today’s session
June 7, 2017
RegMed Investors’ (RMi) closing bell, the sector is strained
June 6, 2017
RegMed Investors’ (RMi) closing bell, the oversold rebounded
June 5, 2017
RegMed Investors’ (RMi) closing bell, even ASCO can’t shake negative sentiment
June 3, 2017
RegMed Investors’ (RMi) closing bell, a two day recovery
June 1, 2017
RegMed Investors’ (RMi) closing bell, an exuberant updraft
35 companies, 1 interpreter!
Insight, foresight and recommendation
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