uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 10, 2017
RegMed Investors’ (RMi) closing bell, the sector stutter steps …
June 29, 2017
RegMed Investors’ (RMi) closing bell, volatility sweeps the sector
June 26, 2017
RegMed Investors’ (RMi) closing bell, what news as the sector stays up …
June 23, 2017
RegMed Investors’ (RMi) closing bell, staying up with momentum
June 22, 2017
RegMed Investors’ (RMi) closing bell, still in a sprint mode with strong gains
June 21, 2017
RegMed Investors’ (RMi) closing bell, some substantial gains
June 20, 2017
RegMed Investors’ (RMi) closing bell, Icarus is soaring
June 19, 2017
RegMed Investors’ (RMi) closing bell, it was time for the upside to shine
June 17, 2017
RegMed Investors’ (RMi) closing bell, the road ahead is barely paved
June 15, 2017
RegMed Investors’ (RMi) closing bell, the pressure is still on
35 companies, 1 interpreter!
Insight, foresight and recommendation
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