uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 17, 2017
RegMed Investors’ (RMi) closing bell analysis, investors should reflect about what to do next
January 13, 2017
RegMed Investors’ (RMi) closing bell analysis, the week of hype was cut short
January 12, 2017
RegMed Investors’ (RMi) closing bell analysis, 2017 is starting off on a "fractured foot"
January 11, 2017
RegMed Investors’ (RMi) mid-day analysis, the sector gets a message nailed to the door …
January 10, 2017
RegMed Investors’ (RMi) closing bell analysis, some of the “dogs” of sector are getting sheared
January 9, 2017
RegMed Investors’ (RMi) closing bell analysis, the conference week that sets the tone of 2017 or does it?
January 6, 2017
RegMed Investors’ (RMi) closing bell analysis, sector dumps to the downside
January 5, 2017
RegMed Investors’ (RMi) closing bell analysis, weakness ripped the upside a new one
December 19, 2016
RegMed Investors’ (RMi) closing bell analysis, the usual suspects …
December 16, 2016
RegMed Investors’ (RMi) closing bell analysis, the option witch was on its broom …
35 companies, 1 interpreter!
Insight, foresight and recommendation
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