uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 2, 2016
Regenerative Medicine Earnings Scorecard - Q3/2016 - to date
November 1, 2016
RegMed Investors’ (RMi) closing bell analysis, appreciation is welcomed back
October 17, 2016
RegMed Investors’ (RMi) closing bell analysis, the wall of worry heightens
September 29, 2016
RegMed Investors’ closing bell analysis, we’ve seen this movie before
September 23, 2016
RegMed Investors’ closing bell analysis, what’s the wrong side of the trade these days?
September 22, 2016
RegMed Investors’ closing bell analysis, the pace of sustainability in the sector …
September 16, 2016
RegMed Investors’ closing bell analysis, the quadruple witch did not fly too high
September 15, 2016
RegMed Investors’ closing bell analysis, volatility puts a hex on upside pricing
September 2, 2016
RegMed Investors’ closing bell analysis, what’s an investor? An investor is a trader that is underwater.
August 31, 2016
RegMed Investors’ closing bell analysis, investors should have been ready as I had stated – the sector was vulnerable!
35 companies, 1 interpreter!
Insight, foresight and recommendation
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