uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
December 4, 2015
RegMed’s close: volatility widens the gap in performance
December 2, 2015
RegMed’s close: What’s there to look forward to ...
December 2, 2015
Higher open expected. RegMed’s pre-open - confusing and mixed signals
December 1, 2015
RegMed’s close: weakness trumps expectation after a week of ups
December 1, 2015
Positive open expected. RegMed’s pre-open, “our” universe is a riddled with dysfunction
November 30, 2015
RegMed’s close: The sector can’t hide from a few things …
November 27, 2015
RegMed’s close: what’s more dangerous than the lesson of price swing bubbles?
November 24, 2015
RegMed’s close: another knee- jerk reaction
November 17, 2015
A positive open is expected. RegMed’s pre-open, pricing sustainability has become a challenge as even traders become pickier
November 16, 2015
RegMed’s close: a day of anything goes and it did, then the sector ended neutral
35 companies, 1 interpreter!
Insight, foresight and recommendation
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