uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 16, 2015
Regenerative Medicine Earnings Scorecard - Q3/2015
November 11, 2015
RegMed’s close: sentiment is flashing danger signals
November 5, 2015
RegMed’s close: as the sector balloon deflates, BLUE takes a BIG hit joined by JUNO, ONCE, QURE and KITE
November 5, 2015
RegMed’s mid-day: support breaks down
November 5, 2015
Higher open expected. RegMed’s pre-open, defining the probabilities after three good days
November 4, 2015
RegMed’s close: retreating, reversing and reverting to maintain gains
November 3, 2015
RegMed’s close: piloting the portfolio, the pricing pattern is full
November 2, 2015
RegMed’s close: another wild swing, a short-term feeding frenzy?
October 28, 2015
RegMed’s close: a fickle sector smells of too much short-term-ism
October 27, 2015
RegMed’s close: the sector is caught in limbo stuck between markets, time to financial results, the FED and expectation
35 companies, 1 interpreter!
Insight, foresight and recommendation
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