uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 26, 2015
RegMed’s close: the need to recoup losses is greater than ever
October 26, 2015
Lower open expected. RegMed’s pre-open, we’re ready for an upside
October 21, 2015
RegMed’s close: the tipping or tilting point
October 21, 2015
RegMed’s mid-day: Athersys (ATHX) sets a domino effect as the sector suffers
October 20, 2015
RegMed’s close: same story, different day, traders are in until they're out
October 19, 2015
RegMed’s close: low volume, fear, migrating momentum and obfuscated indicators
October 16, 2015
RegMed’s close: gains evaporate as fear and de-risking return while options expire ahead of the weekend?
October 12, 2015
RegMed’s close: a quasi-holiday, narrow ranges, indexes and ETFs are spotty – indecision or boredom?
October 7, 2015
RegMed’s close: what’s supporting today’s “bounce”? It's still going to be a battleground!
October 6, 2015
Lower open expected; RegMed, got stamina – gear-up for a harsh topography?
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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