uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 25, 2015
RegMed’s close: a strong beginning slipped to a good ending
August 21, 2015
RegMed’s close: be careful, dip buyers will become rally sellers
August 19, 2015
Lower open expected; RegMed’s suffering a “death by a thousand cuts”
August 18, 2015
RegMed’s close: momentum’s fast, volatility’s high translating into weakness signals
August 18, 2015
RegMed’s mid-day: I am interested in “why” a stock trades at a given price and even more interested in where it may be headed next.
August 17, 2015
RegMed’s close: traded up leap-frogging two day’s downs
August 17, 2015
Flat open expected; RegMed hopes to avoid another ambush
35 companies, 1 interpreter!
Insight, foresight and recommendation
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