uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 17, 2015
RegMed’s close: headline, rates remain unchanged; “our” reality is the short side offers the strongest opportunity
September 16, 2015
RegMed’s close: from the down side, to a neutral mid-day and then closing up, what now brown cow?
September 15, 2015
RegMed’s close: The market hates uncertainty and the trading range of sector trends obliterate any semblance of consistency
September 8, 2015
RegMed’s close: the sector is hot but, is it accelerating to be overbought? I wouldn’t be buying but, consolidating some gains
September 8, 2015
RegMed’s mid-day: wild sector ride, I think it's just a temporary high, wait for a sentiment and strength “flush”
September 3, 2015
RegMed’s close: The connection between causation and connection - three down follow three up days, speaks to functional dependencies?
September 2, 2015
RegMed’s close: stocks jumped, trying to recover from the last two day’s downdraft
September 1, 2015
RegMed’s mid-day: the vulnerability of the sector is worrisome as technicals are challenged
August 31, 2015
RegMed’s close: oversold, overbought and smacked down; the equity risk is spring loaded after last week’s roller-coaster ride
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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