uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 16, 2015
RegMed’s close, traders are now in control of sentiment but, it’s artificial
July 16, 2015
uniQure (QURE) new SVP of R&D
July 13, 2015
RegMed’s mid-day: a bit of optimism as we climb out-of-the-hole!
July 10, 2015
RegMed, so what can you promise investors – next week?
July 10, 2015
RegMed’s mid-day:headwinds are receding but, still scary
July 9, 2015
RegMed’s mid-day: uncertainty created a waiting game with an oversold bounce outgoing – another I told you so!
July 8, 2015
RegMed fell further after wrestling with the oversold gorilla
July 7, 2015
RegMed’s mid-day: mismanaged price targets allow speculators to nibble the edges of value
July 7, 2015
Higher open expected; RegMed has a lot of head fakes
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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