uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 6, 2015
RegMed, the chilling effect - the dynamics keep moving – volume, volatility based on the probabilities of fear
July 6, 2015
RegMed’s mid-day: tone down the geo-political noise, as SCG&RM equities snap back albeit slowly
July 5, 2015
RegMed, what’s a weekend without a wrap-up; thanks for holiday spirits, it loosens the pain of losses
July 2, 2015
RegMed, sentiment and uncertainty are weighing on the market
July 2, 2015
Higher open expected; RegMed, wide, loose and erratic price swings
July 1, 2015
Adding coverage
July 1, 2015
Higher open expected; RegMed, the sector takes the elevator down and the stairs up
June 8, 2015
Regenerative Medicine Earnings Scorecard - Q2/2015
June 4, 2015
Regenerative Medicine Earnings Scorecard - Q1/2015
35 companies, 1 interpreter!
Insight, foresight and recommendation
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