uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 9, 2022
RegMed Investors’ (RMi) closing bell: something had to give, just too many earnings’ losses and missed revenue estimates
August 8, 2022
RegMed Investors’ (RMi) closing bell: sector rebounds from gutter to sidewalk action with lack luster earnings’ results
August 8, 2022
RegMed Investors’ (RMi) pre-open: as the upside party rages on, is sector share pricing support solid?
August 5, 2022
RegMed Investors’ (RMi) closing bell: follow the bouncing share pricing as acquisition re-heats sector
August 4, 2022
RegMed Investors’ (RMi) closing bell: gravity was not a downward force as anticipated
August 3, 2022
RegMed Investors’ (RMi) closing bell: the sector parties to the upside, the question is what happens when the music ends
August 3, 2022
RegMed Investors’ (RMi) pre-open: earnings and more earnings with a few shots-in -the dark
August 1, 2022
RegMed Investors’ (RMi) closing bell: an end of month tumble on Friday, a stumble on Monday, the first session of August
July 29, 2022
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector tumbles
July 28, 2022
RegMed Investors’ (RMi) closing bell: a focus on long-term investments will ruin short and near-term portfolio performance
35 companies, 1 interpreter!
Insight, foresight and recommendation
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