uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 28, 2022
RegMed Investors’ (RMi) pre-open: wrapping-up a rough week for beaten down cell and gene therapy equities
January 27, 2022
RegMed Investors’ (RMi) closing bell: the costs of the roller-coaster sector rides
January 26, 2022
RegMed Investors’ (RMi) closing bell: I loved the smell of appreciation in the morning until the algorithms napalmed the cell and gene therapy sector
January 25, 2022
RegMed Investors’ (RMi) closing bell: wild volatility charges the slips and slides as the sector’s come-back collapses
January 25, 2022
RegMed Investors’ (RMi) pre-open: wait, one dramatic and wild session with recovery does not make a sustainable sector
January 24, 2022
RegMed Investors’ (RMi) closing bell: panic sector selling and then a major comeback
January 21, 2022
RegMed Investors’ (RMi) pre-open: waiting for the bottom achievement after the past week’s fizzles
January 20, 2022
RegMed Investors’ (RMi) closing bell: finally, the oversold were appreciative until the lower reverse unfolded
January 19, 2022
RegMed Investors’ (RMi) closing bell: a tightening cycle
January 14, 2022
RegMed Investors’ (RMi) closing bell: a late session rebound, a bouncing sector rotates to close positive
35 companies, 1 interpreter!
Insight, foresight and recommendation
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Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors
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