uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
January 12, 2022
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector went off the road and into a ditch, again
January 12, 2022
RegMed Investors’ (RMi) pre-open: cause and effect follow a weak aftermarket
January 11, 2022
RegMed Investors’ (RMi) closing bell: sector volatility works to our favor in this market
January 11, 2022
RegMed Investors’ (RMi) pre-open: sector leadership, the few and the far between
January 10, 2022
RegMed Investors’ (RMi) closing bell: I’m not too early for the oversold party as I had written “it’s time to take a few risks”
January 7, 2022
RegMed Investors’ (RMi) pre-open: will there be a finger that fits in this leaking and spiraling dyke, Hans Brinker where are you?
January 6, 2022
RegMed Investors’ (RMi) closing bell: confluences, a junction of two positions of thought on the cell and gene therapy sector, BUY or SELL?
January 6, 2022
RegMed Investors’ (RMi) pre-open: riding the waves in which direction after two (2) sessions of carnage?
January 3, 2022
RegMed Investors’ (RMi) closing bell: starting 2022 with a flash of confidence
35 companies, 1 interpreter!
Insight, foresight and recommendation
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