uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 24, 2025
RMi Closing Bell: Restoring
October 24, 2025
RMi pre-open: CPI
October 23, 2025
RMi Closing Bell: Another negative
October 22, 2025
RMi Closing Bell: Wipe-out
October 22, 2025
RMi pre-open: Impressions
October 21, 2025
RMi Closing Bell: Fleeing
October 21, 2025
RMi pre-open: Caution
October 20, 2025
RMi Closing Bell: Rational exuberance
October 20, 2025
RMi pre-open: Offense
October 17, 2025
RMi Closing Bell: Wobbling
35 companies, 1 interpreter!
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