uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
July 3, 2025
RegMed Investors (RMi) Closing Bell: Feeling the high, just haven’t exhaled yet
July 1, 2025
RegMed Investors (RMi) Closing Bell: the wall of worry was scaled
June 30, 2025
RegMed Investors (RMi) Closing Bell: the sword hung by a single horsehair, implying an ever-present peril facing share pricing
June 27, 2025
RegMed Investors (RMi) Closing Bell: Econ’s inflation data was hotter than expected as May PCE pushes rate cuts odds lower
June 26, 2025
RegMed Investors (RMi) Closing Bell: Econs cried havoc and let slip the algo dogs of electronic trading
June 25, 2025
RegMed Investors (RMi) Closing Bell: Electronic trading slipped in to minimize earlier share pricing blast circumference
June 24, 2025
RegMed Investors (RMi) Closing Bell: clicking on the after burners
June 24, 2025
RegMed Investors’ (RMi) pre-open: get it up
June 23, 2025
RegMed Investors (RMi) Closing Bell: Sector has minor collateral damage
June 23, 2025
RegMed Investors’ (RMi) pre-open: controlled response of bomb futures
35 companies, 1 interpreter!
Insight, foresight and recommendation
My motto … never leave an investor uninformed! I say today what others won’t, so you can do what others can’t.
My name is Henry McCusker; I endorse these opinions under my own name and with a subscription based membership.
Do you have an opinion you would like to share with us? We would like to hear from you.
Please e-mail us at hwm@regmedinvestors.com.
Editor and Publisher ... Henry McCusker enters his tenth (10th) year at RegMed Investors