uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
August 23, 2021
RegMed Investors’ (RMi) closing bell: are we chasing the oversold?
August 19, 2021
RegMed Investors’ (RMi) closing bell: a bubblicious session
August 18, 2021
RegMed Investors’ (RMi) closing bell: another early rout but, with no comeback in the cell and gene therapy sector
August 17, 2021
RegMed Investors’ (RMi) closing bell: a rout with a late session comeback in the cell and gene therapy sector
August 17, 2021
RegMed Investors’ (RMi) pre-open: buying weakness is still early and speculative yet, timing is everything
August 16, 2021
RegMed Investors’ (RMi) closing bell: starting the week, the cell and gene therapy sector exhibits an irregular pulse and heartbeat
August 13, 2021
RegMed Investors’ (RMi) closing bell: sector wavers with minimal percentage movement, low volume and lack of breath
August 12, 2021
RegMed Investors’ (RMi) closing bell: cell and gene therapy sector flips positive at mid-day
August 11, 2021
RegMed Investors’ (RMi) closing bell: volatility sucks pond water
August 11, 2021
RegMed Investors’ (RMi) pre-open: how do you know, what will happen today if you don’t have a handle on yesterday
35 companies, 1 interpreter!
Insight, foresight and recommendation
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