uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
September 9, 2021
RegMed Investors’ (RMi) closing bell: sentiment loads its soppiness
September 8, 2021
RegMed Investors’ (RMi) pre-open: more volatility and some bounces
September 7, 2021
RegMed Investors’ (RMi) closing bell: drip, drip down
September 7, 2021
RegMed Investors’ (RMi) pre-open: through looking glass, what does one see?
September 3, 2021
RegMed Investors’ (RMi) closing bell: the cell and gene therapy highs hit the wall and bounced to the downside
September 2, 2021
RegMed Investors’ (RMi) closing bell: strolling to the upside on low volume
August 30, 2021
RegMed Investors’ (RMi) closing bell: the cell and gene therapy sector’s upside collapsed as the session progressed
August 27, 2021
RegMed Investors’ (RMi) closing bell: sector pops on rotation to biotech/healthcare
August 26, 2021
RegMed Investors’ (RMi) closing bell: a challenging session fraught with sorrow
August 25, 2021
RegMed Investors’ (RMi) closing bell: investors do not have an easy consensus as rebounds come and then go
35 companies, 1 interpreter!
Insight, foresight and recommendation
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