uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 4, 2021
RegMed Investors’ (RMi) closing bell: depths and peaks as experienced by the week
June 4, 2021
RegMed Investors’ (RMi) pre-open: trends and trajectories are just too speculative
June 3, 2021
RegMed Investors’ (RMi) closing bell: cell and gene therapy pricing action sprung a hole in the dike
June 2, 2021
RegMed Investors’ (RMi) closing bell: cell and gene therapy trips over the falling sentiment
June 1, 2021
RegMed Investors’ (RMi) closing bell: definitely not a cell and gene therapy sector day
May 28, 2021
RegMed Investors’ (RMi) closing bell: wrapping the week on a weak note
May 28, 2021
RegMed Investors’ (RMi) pre-open: escape, escape
May 27, 2021
RegMed Investors’ (RMi) closing bell: sector stocks are rising in a relatively back and forth session
May 25, 2021
RegMed Investors’ (RMi) closing bell: sector needs a blue pill to increase its confidence
May 24, 2021
RegMed Investors’ (RMi) closing bell: interest or the lack thereof in the cell and gene therapy sector
35 companies, 1 interpreter!
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