uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
June 15, 2021
RegMed Investors’ (RMi) closing bell: the sector stampeded to the downside, told you so!
June 15, 2021
RegMed Investors’ (RMi) pre-open: are you ready …
June 14, 2021
RegMed Investors’ (RMi) closing bell: winner, winner, chicken dinner
June 11, 2021
RegMed Investors’ (RMi) closing bell: another positive session to end the week
June 11, 2021
RegMed Investors’ (RMi) pre-open: the sector revels in news
June 10, 2021
RegMed Investors’ (RMi) closing bell: the trend is still the cell and gene therapy’s sector friend
June 8, 2021
RegMed Investors’ (RMi) closing bell: barely trimming the upside while volume remains weak
June 7, 2021
RegMed Investors’ (RMi) closing bell: not crying about the sector high
June 7, 2021
RegMed Investors’ (RMi) pre-open: risk, not too hot but, not to cool to ponder moves
35 companies, 1 interpreter!
Insight, foresight and recommendation
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