uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 12, 2020
RegMed Investors’ (RMi) pre-open: a sector of choices but, at a cost as “eyes” are elsewhere
November 11, 2020
RegMed Investors’ (RMi) closing bell: the daily trend turned to be a friend
November 10, 2020
RegMed Investors’ (RMi) closing bell: rotation, rations and then exhibits causation of an upside
November 9, 2020
RegMed Investors’ (RMi) closing bell: volatility swings and then disperses the Nasdaq
November 6, 2020
RegMed Investors’ (RMi) closing bell: sector dips after a four-session streak
November 6, 2020
RegMed Investors’ (RMi) pre-open: yesterday, I wrote “bank” profits from highs
November 5, 2020
RegMed Investors’ (RMi) closing bell: realizing upside only comes from selling the risk
November 5, 2020
RegMed Investors’ (RMi) pre-open: calling an audible
November 4, 2020
RegMed Investors’ (RMi) closing bell: wow, momentum rolls sector skyward
November 3, 2020
RegMed Investors’ (RMi) closing bell: markets need election clarity, whether we individually like it or not
35 companies, 1 interpreter!
Insight, foresight and recommendation
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