uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
November 20, 2020
RegMed Investors’ (RMi) pre-open: worsening infections overshadow any semblance of confidence
November 19, 2020
RegMed Investors’ (RMi) closing bell: sector closes positive after a mid-day flop
November 18, 2020
RegMed Investors’ (RMi) closing bell: a late afternoon sell-off
November 18, 2020
RegMed Investors’ (RMi) pre-open: watch the patterns, Advance/Decline (A/D) lines are slipping
November 17, 2020
RegMed Investors’ (RMi) closing bell: the upside was poured into a less than half-empty sector glass
November 17, 2020
RegMed Investors’ (RMi) pre-open: is the sector recognized as a glass-half-full, half-empty or ready for a new pour?
November 16, 2020
RegMed Investors’ (RMi) closing bell: hurrah to gains yet, confidence is still on the edgy side
November 13, 2020
RegMed Investors’ (RMi) closing bell: closing the sector’s week positivity after all the sour sentiment
November 13, 2020
RegMed Investors’ (RMi) pre-open: a Friday high?
November 12, 2020
RegMed Investors’ (RMi) closing bell: where there was a spark became a sector fire to close negative
35 companies, 1 interpreter!
Insight, foresight and recommendation
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