uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 22, 2020
RegMed Investors’ (RMi) closing bell: sector rises after being oversold
October 22, 2020
RegMed Investors’ (RMi) pre-open: volatility “ain’t” leaving
October 21, 2020
RegMed Investors’ (RMi) closing bell: sector dances the limbo; how low can it go?
October 20, 2020
RegMed Investors’ (RMi) closing bell: the hole in the sector just got deeper
October 20, 2020
RegMed Investors’ (RMi) pre-open: volatility is a double edge knife
October 16, 2020
RegMed Investors’ (RMi) closing bell: a churning week – pockets of strength with a ending daily and solid sector showing
October 15, 2020
RegMed Investors’ (RMi) closing bell: what’s the next catalyst for the sector and markets
October 14, 2020
RegMed Investors’ (RMi) closing bell: returning to a deepening downside
October 13, 2020
RegMed Investors’ (RMi) closing bell: sector closed positive after lower moves
35 companies, 1 interpreter!
Insight, foresight and recommendation
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