uniQure N.V., a biopharmaceutical company, develops adeno-associated virus (AAV) based gene therapies through its technology platform for multiple therapeutic areas. The company offers Glybera for the treatment of patients with lipoprotein lipase deficiency. It also develops AMT-060, a gene therapy that is in Phase I/II clinical trial for the treatment of hemophilia B; S100A1, a preclinical therapeutic for congestive heart failure; AMT-021, a gene therapy, which has completed Phase I clinical trial for acute intermittent porphyria; AMT-110, a gene therapy that is in Phase I/II clinical trial for Sanfilippo B syndrome; and AAV2/glial cell line-derived neurotrophic factor for Parkinson's disease. The company has collaborations with Chiesi Farmaceutici S.p.A., Digna Biotech, Institut Pasteur, University of California San Francisco, Bristol-Myers Squibb, and 4D Molecular Therapeutics. uniQure N.V. was founded in 1998 and is headquartered in Amsterdam, the Netherlands.
October 13, 2020
RegMed Investors’ (RMi) pre-open: I’m tagging the risk candidates as new highs enhance portfolio profiting
October 12, 2020
RegMed Investors’ (RMi) closing bell: speculation primes the market pump, dime it
October 9, 2020
RegMed Investors’ (RMi) closing bell: headed to the weekend with a smile from the market and a stuffed olive in the libation
October 8, 2020
RegMed Investors’ (RMi) closing bell: slipping and squeaking to a positive close
October 7, 2020
RegMed Investors’ (RMi) closing bell: stay on track, go with the flow until it ceases
October 5, 2020
RegMed Investors’ (RMi) closing bell: what a difference a session makes
October 2, 2020
RegMed Investors’ (RMi) closing bell: stocks closed lower after President Trump tests positive for Coronavirus
October 1, 2020
RegMed Investors’ (RMi) closing bell: some equities felt the love
September 30, 2020
RegMed Investors’ (RMi) closing bell: end of September and Q3
September 29, 2020
RegMed Investors’ (RMi) closing bell: slippin’ and slidin’
35 companies, 1 interpreter!
Insight, foresight and recommendation
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